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18-10-2022 | Neurology | Video

Favorable treatment outcomes in patients with SMA diagnosed through newborn screening

Peter Karachunski reports the findings from a real-world study showing that disease-modifying therapies have favorable safety and effectiveness profiles in infants with spinal muscular atrophy identified through newborn screening (3:40).

Funding for independent interviews at WMS 2022 was provided by F. Hoffmann-La Roche Ltd, Basel, Switzerland.