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20-10-2022 | Neurology | Video

microRNAs linked to nusinersen response in SMA

Sharon Aharoni talks us through the results of a study showing that lower baseline levels of two muscle microRNAs measured in the cerebrospinal fluid are associated with better clinical response to nusinersen treatment in patients with type 2 or 3 spinal muscular atrophy (3:00).

Funding for independent interviews at WMS 2022 was provided by F. Hoffmann-La Roche Ltd, Basel, Switzerland.