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08-05-2019 | Motor neuron diseases | Video

AAN 2019: Promising early results for risdiplam in babies with type 1 SMA

Laurent Servais reports on part 1 of the FIREFISH trial of risdiplam in infants with type 1 spinal muscular atrophy showing improvements in various outcomes, including motor function and ventilation (3:55).

Funding for this video was provided by F. Hoffmann-La Roche Ltd, Basel, Switzerland.

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